Gene therapy article published by representatives from hemophilia patient organizations

Gene therapy has held the promise of a potential cure for hemophilia for a long time. For this reason, many people with hemophilia have been following the progress of this treatment very closely, including the six authors of an article published this month, who emphasize the need for transparency and caution as we move forward with clinical trials and science. Gene therapy to cure haemophilia: Is robust scientific inquiry the missing factor? was published in Haemophilia, the official journal of the WFH, and authored by representatives of major hemophilia patient organizations: Glenn Pierce, MD, PhD, WFH VP Medical, Radoslaw Kaczmarek, Polish Hemophilia Society, Declan Noone, European Hemophilia Consortium, Brian O’Mahony, Irish Haemophilia Society, David Page, Canadian Hemophilia Society and Mark W. Skinner, National Hemophilia Foundation (U.S.A). To read the article, please click here.