WFH NETWORK

Gene therapy: Is robust scientific inquiry the missing factor?

Date, time: Friday, December 11 at 10:00 a.m. EST (15:00 UTC/GMT)

Zoom link: https://us02web.zoom.us/webinar/register/WN_B-1KYKY1QAqjYYUN1mwP2A

On Friday, December 11 at 10:00 a.m. EST (15:00 UTC/GMT), the World Federation of Hemophilia (WFH) will host a 60-minute interactive session to explore patient perspectives related to scientific inquiry of gene therapy.

David Page from the Canadian Hemophilia Society will be moderating the session. The panelists—who will include Glenn Pierce, MD, PhD, WFH Vice President, Medical, Radoslaw Kaczmarek, Polish Hemophilia Society, Declan Noone, European Hemophilia Consortium, Brian O’Mahony, Irish Haemophilia Society, and Mark W. Skinner, National Hemophilia Foundation (U.S.A)—are following the science of gene therapy and have called for transparency in the scientific quest to answer the unknowns around safety, variability and durability of response in their publication Gene therapy to cure haemophilia: Is robust scientific inquiry the missing factor? which was recently published in Haemophilia, the official journal of the WFH.

We encourage you to submit questions in advance by emailing the WFH at [email protected], no later than Wednesday, December 9. Participants will also have the opportunity to ask questions during the session and presenters will do their best to answer them all—time permitting.