WFH Statement
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WFH supports MASAC’s recommendation on the risks of gene therapy trials for hemophilia
On December 6, 2018, MASAC—the NHF’s Medical and Scientific Advisory Council—published recommendation #254, entitled, “MASAC Document Regarding Risks of Gene Therapy Trials for Hemophilia”. MASAC’s recommendation...
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WFH Medical Advisory Board (MAB) supports MASAC’s recommendation on the use and management of emicizumab-kxwh (Hemlibra®) for hemophilia A with and without inhibitors
On December 6, 2018, MASAC—the NHF’s Medical and Scientific Advisory Council—published recommendation #255 entitled, “Recommendation on the Use and Management of Emicizumab-kxwh (Hemlibra®) for Hemophilia...
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Alnylam Suspends Fitusiran Dosing due to Thrombotic Event in Phase 2 open-label extension study
The WFH was saddened to learn of the death of a hemophilia A patient taking part in the Phase II trial of fitusiran, in development...
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Roche statement on emicizumab clinical trial adverse event
Roche has released the following statement to the WFH following the death of a patient in a clinical trial. The WFH expresses our sincere condolences...
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WFH STATEMENT on SIPPET Study Results
The results of the SIPPET (Survey of Inhibitors in Plasma-Products Exposed Toddlers) study were published May 26, 2016 in the New England Journal of Medicine....
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SIPPET study results published in New England Journal of Medicine
May, 2016 – The results of the SIPPET (Survey of Inhibitors in Plasma-Products Exposed Toddlers) study were published today in the New England Journal of...
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vCJD case reported in patient with a different genotype
The first case of variant Creutzfeldt-Jakob disease (vCJD) in a patient that is genetically different from all previous confirmed cases has been been reported in...
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EMA investigating rare adverse events associated with hepatitis C treatment
The European Medicines Agency (EMA) has started a review of medicines known as direct-acting antivirals used for treating chronic hepatitis C infection. There have been...
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World Federation of Hemophilia product selection statement
The selection of safe, effective medicinal products is the responsibility of national regulatory and health agencies. In the case of clotting factor concentrates, whether plasma-derived...
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WFH statement on end-product testing
End-product testing cannot be used to assure viral safety of clotting factor concentrates. The testing used for screening plasma for viral agents, whether performed on...
